News RSS Bioethics News.


Gene therapy makes a big advance treating hemophilia B blood disorder

External Link - Source: Washington Post

Konduros, 53, who runs a bakery and cafe in southeastern Ontario, is one of 10 men in an early-stage trial sponsored by Spark Therapeutics. (The disorder is much more common in men than women.) On Wednesday, researchers reported that a single intravenous infusion of Spark’s novel gene therapy enabled patients to safely produce sufficient clotting factor to prevent dangerous bleeding episodes.

This entry was posted in Clinical Trials & Studies and tagged . Bookmark the permalink.